Peking University scientists have developed a cancer therapy that could make life-saving treatment accessible to any patient, ...

An experimental gene therapy that turns a patient's own blood cells into cancer killers worked in a major study, with more than one-third of very sick lymphoma patients showing no sign of disease six ...

As AAV9 and CRISPR programs navigate safety, delivery and scalability hurdles, small molecules offer a deployable, scalable ...

The commercial success of existing lipid-lowering medications highlights the enormous market potential for effective ...

It can cure deadly diseases, save long-term healthcare costs and transform lives. But the U.S. insurance system still isn’t ...

As other gene editing programs fold or get sold, Arbor Biotechnologies has secured $73.9 million to advance its lead liver-targeting gene therapy into human trials. The series C was led by Arch ...

And it has paved the way for other therapeutic strategies, including the first gene therapy delivered through skin grafts, ...

BEIJING & CAMBRIDGE, Mass--(BUSINESS WIRE)--CANbridge Pharmaceuticals Inc., a biopharmaceutical company developing innovative drug candidates to treat underserved medical conditions, announced that it ...

BOSTON & MONTREAL, September 11, 2025--enGene Holdings Inc. (Nasdaq: ENGN, "enGene" or the "Company"), a clinical-stage, ...