Long-term follow-up shows 95% success rate, no serious complications in largest ADA-SCID gene therapy study to date ...

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the burden of lifelong transfusions. A single one-time gene therapy could free ...

For nearly three decades, Mayo Clinic researcher Christopher Evans, Ph.D., has pushed to expand gene therapy beyond its original scope of fixing rare, single-gene defects. That has meant ...

Mercer County Community College launches an aseptic biomanufacturing program and mobile lab in Trenton to train students for ...