Key signs of spinal muscular atrophy include severe muscle weakness, difficulty breathing or swallowing, and missing ...

SMA is a genetic condition that impacts motor neurons, leading to muscle weakness that affects essential functions like breathing and movement. Treatments like Spinraza and Zolgensma can help manage ...

Hundreds more children with muscle-wasting condition spinal muscular atrophy (SMA) are to be offered potentially “life-changing” therapy on the NHS which could help them live ...

"Our preliminary findings show that German children with SMA, despite significant physical disability, have surprisingly good subjective HRQoL." – Erik Landfeldt, MSc, PhD Previous studies have found ...