Scientists are testing an entirely new way to fight heart disease: whether gene editing might offer a one-time fix for high ...
A research team has successfully demonstrated the world's first gene-editing treatment for Leber's hereditary optic ...
Faced with a life-threatening metabolic disease, KJ’s doctors at Children’s Hospital of Philadelphia sprinted to create a ...
In a Phase 1, first-in-human trial, a one-time infusion of an investigational CRISPR-Cas9 therapy targeting angiopoietin-like protein 3 (ANGPTL3) was safe and reduced LDL cholesterol by nearly 50% and ...
A new skin-applied gene therapy uses lipid nanoparticles to deliver gene editing into skin stem cells, correcting ...
A new gene-editing technique enables the correction of multiple genetic mutations simultaneously, transforming the prospects for millions living with complex inherited diseases, such as cystic ...
San Francisco-based startup Preventive has raised nearly $30 million from investors, including OpenAI CEO Sam Altman and Coinbase CEO Brian Armstrong, to develop embryo gene-editing technology aimed ...
Gene editing is now reaching the mainstream, ushering in a new era of genetic manipulation. Traditionally, inserting or deleting entire genes, regulating their expression, and altering specific ...
A multidisciplinary committee of experts studied the scientific underpinnings of human gene-editing technologies, their potential use in biomedical research and medicine -- including human germline ...